Suspected sepsis in people aged 16 or over: recognition, assessment and early management (NG253)Product type:GuidanceProgramme:NICE guidelinePublished: 19 November 2025
Suspected sepsis in pregnant or recently pregnant people: recognition, diagnosis and early management (NG255)Product type:GuidanceProgramme:NICE guidelinePublished: 19 November 2025
Suspected sepsis in under 16s: recognition, diagnosis and early management (NG254)Product type:GuidanceProgramme:NICE guidelinePublished: 19 November 2025
Garadacimab for preventing recurrent attacks of hereditary angioedema in people 12 years and over (TA1101)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 8 October 2025
Donidalorsen for preventing recurrent attacks of hereditary angioedema in people 12 years and over [ID6457]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: 18 June 2026
Olezarsen for treating familial chylomicronaemia syndrome [ID6585]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: 19 August 2026
Avapritinib for treating inadequately controlled moderate to severe indolent systemic mastocytosis [ID6578]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: 3 September 2026
Plozasiran for treating familial chylomicronaemia syndrome [ID6593]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: 18 November 2026
Concizumab for treating severe haemophilia A or moderate to severe haemophilia B in people 12 years and over without inhibitors [ID5099]Status:Awaiting developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Fidanacogene elaparvovec for treating moderately severe to severe haemophilia B [ID4032]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Apadamtase alfa for treating congenital thrombotic thrombocytopenic purpura caused by ADAMTS-13 deficiency [ID6192]Status:Awaiting developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Ravulizumab for untreated thrombotic microangiopathy after a haematopoietic stem cell transplant in people aged 28 days and over [TSID10642][ID6319]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Sebetralstat for treating acute attacks of hereditary angioedema in people aged 12 and over [ID6284]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Denecimig (Mim8) for preventing bleeding episodes in haemophilia A in people 1 year and over ID6400Status:Awaiting developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Inclacumab for preventing recurrent vaso-occlusive crises in sickle cell disease in people 16 years and over [ID6551]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Mozafancogene autotemcel for treating Fanconi anaemia in people 1 to 17 years [ID12203]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Ferric citrate for managing iron and serum phosphorus levels in anaemia associated with chronic kidney disease [TSID12221]Status:Topic prioritisationProgramme:Technology appraisal guidanceExpected publication date: TBC
Avexitide for treating hypoglycaemia after bariatric surgery [TSID12233]Status:Awaiting developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Lanadelumab for preventing recurrent attacks of hereditary angioedema in people 2 years and over [TSID12298]Status:Topic prioritisationProgramme:Technology appraisal guidanceExpected publication date: TBC
Concizumab for treating haemophilia A or B in people 12 years and over with inhibitors [ID6665]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Sutimlimab for treating haemolytic anaemia in people with cold agglutinin disease [ID6673]Status:Awaiting developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Etavopivat for treating sickle cell disease in people 12 years and over [TSID12320]Status:Awaiting developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Luspatercept for Anaemia due to myelodysplastic syndromes [TSID12310]Status:Awaiting developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Luspatercept for treating anaemia caused by myelofibrosis [TSID12309]Status:Awaiting developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Peginterferon alfa-2a for treating polycythaemia vera or essential thrombocythaemia [TSID12325]Status:Topic prioritisationProgramme:Technology appraisal guidanceExpected publication date: TBC