Arimoclomol for treating Niemann-Pick disease Type C [ID1312]Status:In developmentProgramme:Highly specialised technologies guidanceExpected publication date: TBC
Cardiovascular risk assessment and lipid modificationStatus:In developmentExpected publication date: 23 July 2025
Olipudase alfa for treating Niemann-Pick disease types A and B [ID3913 ]Status:In developmentProgramme:Highly specialised technologies guidanceExpected publication date: TBC
VTS-270 for treating Niemann-Pick type C1 [ID1267]Status:In developmentProgramme:Highly specialised technologies guidanceExpected publication date: TBC