Sodium zirconium cyclosilicate for treating hyperkalaemia (TA1148)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 29 April 2026
Vutrisiran for treating transthyretin amyloidosis with cardiomyopathy (TA1115)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 10 December 2025
Fosdenopterin for treating molybdenum cofactor deficiency type A (terminated appraisal) (TA1078)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 25 June 2025
Somapacitan for treating growth hormone deficiency in people 3 to 17 years (TA1066)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 3 June 2025
Eplontersen for treating hereditary transthyretin-related amyloidosis (TA1020)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 27 November 2024
Burosumab for treating X-linked hypophosphataemia in adults (TA993)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 7 August 2024
Tafamidis for treating transthyretin amyloidosis with cardiomyopathy (TA984)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 19 June 2024
Daratumumab in combination for treating newly diagnosed systemic amyloid light-chain amyloidosis (TA959)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 27 March 2024
Pegunigalsidase alfa for treating Fabry disease (TA915)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 4 October 2023
Cipaglucosidase alfa with miglustat for treating late-onset Pompe disease (TA912)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 15 August 2023
Mitapivat for treating pyruvate kinase deficiency (terminated appraisal) (TA867)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 16 February 2023
Vutrisiran for treating hereditary transthyretin-related amyloidosis (TA868)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 15 February 2023
Slow-release potassium bicarbonate–potassium citrate for treating distal renal tubular acidosis (terminated appraisal) (TA838)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 2 November 2022
Avalglucosidase alfa for treating Pompe disease (TA821)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 24 August 2022
Sapropterin for treating hyperphenylalaninaemia in phenylketonuria (TA729)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 22 September 2021
Patiromer for treating hyperkalaemia (TA623)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 13 February 2020