Rebisufligene etisparvovec for treating mucopolysaccharidosis type IIIA ID6540Status:In development | In consultationProgramme:Technology appraisal guidanceConsultation end date: 1 April 2026Expected publication date: TBC
Elamipretide for treating Barth syndrome in people of any age [ID6545]Status:In development | In consultationProgramme:Technology appraisal guidanceConsultation end date: 31 March 2026Expected publication date: TBC