Notice of Appeal
Cerliponase alfa for treating neuronal ceroid lipofuscinosis type 2 (MA review of HST12) [ID6145]
NICEhas received 2 appeals, that fall within one or more of the two strictly limited grounds for appeal, against the Final Draft Guidance on the above technology from the following organisations:
- BioMarin UK Limited
- Batten Disease Family Association CIO (BDFA)
The appeal panel will convene on Tuesday 25 November 2025 at 10:00am via Zoom to hear oral representations from the appellants.
Members of the public, including consultees and commentators for this appraisal, and the press, may request to attend the hearing.
Where possible, requests to attend should be made using the registration link that will be available on our website from Thursday 2 October 2025. The registration period for this appeal will end at 4:00pm on Thursday 18 November 2025.
Further details relating to public attendance at this appeal are available on the same webpage as above.