In development: Guidance, quality standards and advice
Showing 11 to 12 of 12
Title | Type | Expected publication date |
---|---|---|
Tofersen for treating amyotrophic lateral sclerosis caused by SOD1 gene mutations [ID3767] | Highly specialised technology | TBC |
VTS-270 for treating Niemann-Pick type C1 [ID1267] | Highly specialised technology | TBC |