Drisapersen for the first-line treatment of Duchenne's muscular dystrophy [ID911]
In development [GID-HST10004] Expected publication date: TBC
In development [GID-HST10004] Expected publication date: TBC
In development [GID-HST10007] Expected publication date: TBC
In development [GID-NG10052] Expected publication date: TBC
In development [GID-CGWAVE0773] Expected publication date: TBC
In development [GID-NG10059] Expected publication date: TBC
In development [GID-CGWAVE0771] Expected publication date: TBC
In development [GID-NG10141] Expected publication date: 17 November 2021
Proposed [GID-HST10034] Expected publication date: TBC
Proposed [GID-HST10020] Expected publication date: TBC
In development [GID-NG10112] Expected publication date: 16 November 2021
In development [GID-NG10110] Expected publication date: TBC
Proposed [GID-HST10019] Expected publication date: TBC
In development [GID-HST10010] Expected publication date: TBC
In development [GID-HST10017] Expected publication date: TBC
In development [GID-HST10028] Expected publication date: 13 August 2021
In development [GID-NG10127] Expected publication date: 10 August 2022
In development [GID-NG10173] Expected publication date: TBC
In development [GID-NG10164] Expected publication date: 11 May 2022
In development [GID-NG10118] Expected publication date: 30 June 2021
In development [GID-NG10096] Expected publication date: 11 August 2021
In development [GID-NG10145] Expected publication date: 27 April 2022
In development [GID-NG10156] Expected publication date: TBC
In development [GID-NG10176] Expected publication date: 23 March 2023
In development [GID-NG10109] Expected publication date: 09 June 2021
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In development [GID-HST10026] Expected publication date: 25 March 2021
In development [GID-NG10160] Expected publication date: TBC
In development [GID-NG10152] Expected publication date: TBC
Proposed [GID-HST10037] Expected publication date: TBC
Proposed [GID-HST10030] Expected publication date: TBC
In development [GID-LYSOSOMALACIDLIPASEDEFICIENCYSEBELIPASEALFAID737] Expected publication date: TBC
In development [GID-HST10009] Expected publication date: TBC
In development [GID-NG10163] Expected publication date: TBC
In development [GID-NG10178] Expected publication date: 19 April 2023
In development [GID-NG10177] Expected publication date: 19 April 2023
In development [GID-NG10159] Expected publication date: TBC
In development [GID-NG10120] Expected publication date: 17 June 2021
In development [GID-NG10153] Expected publication date: 20 July 2022
Proposed [GID-HST10039] Expected publication date: TBC
In development [GID-NG10175] Expected publication date: 14 December 2022
In development [GID-NG10070] Expected publication date: 07 April 2021
In development [GID-NG10166] Expected publication date: TBC
Proposed [GID-HST10022] Expected publication date: TBC
In development [GID-NG10135] Expected publication date: 02 March 2021
In development [GID-HST10032] Expected publication date: TBC
In development [GID-HST10033] Expected publication date: TBC
Proposed [GID-HST10038] Expected publication date: TBC
In development [GID-NG10107] Expected publication date: 10 February 2021
In development [GID-NG10113] Expected publication date: 19 January 2022