Migalastat for treating Fabry disease (HST4)
Evidence-based recommendations on migalastat (Galafold) for treating Fabry disease in people over 16
Search results
490 results
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Cerliponase alfa for treating neuronal ceroid lipofuscinosis type 2 (HST12)
Evidence-based recommendations on cerliponase alfa (Brineura) for treating neuronal ceroid lipofuscinosis type 2 in children
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Voretigene neparvovec for treating inherited retinal dystrophies caused by RPE65 gene mutations (HST11)
Evidence-based recommendations on voretigene neparvovec (Luxturna) for RPE65-mediated inherited retinal dystrophies in people with vision loss caused by inherit
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Patisiran for treating hereditary transthyretin amyloidosis (HST10)
Evidence-based recommendations on patisiran (Onpattro) for treating hereditary transthyretin amyloidosis in adults with stage 1 and stage 2 polyneuropathy
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Inotersen for treating hereditary transthyretin amyloidosis (HST9)
Evidence-based recommendations on inotersen (Tegsedi) for stage 1 and stage 2 polyneuropathy in adults with hereditary transthyretin amyloidosis
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VTS-270 for treating Niemann-Pick type C1 (ID1267)
Proposed [GID-HST10020] Expected publication date: TBC
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Setmelanotide for treating obesity caused by LEPR or POMC deficiency [ID3764]
Proposed [GID-HST10034] Expected publication date: TBC
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Intrathecal idursulfase for treating Mucopolysaccharidosis type II ID1223
Proposed [GID-HST10019] Expected publication date: TBC
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Velmanase alfa for treating alpha-mannosidosis [ID800]
In development [GID-HST10010] Expected publication date: TBC
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Human alpha1-proteinase inhibitor for treating emphysema ID856
In development [GID-HST10017] Expected publication date: TBC
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Givosiran for treating acute hepatic porphyria [ID1549]
In development [GID-HST10035] Expected publication date: TBC
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Maralixibat for treating type 2 progressive familial intrahepatic cholestasis ID3818
Proposed [GID-HST10040] Expected publication date: TBC
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OTL-101 for treating adenosine deaminase deficiency–severe combined immunodeficiency [ID1152]
Proposed [GID-HST10022] Expected publication date: TBC
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Lysosomal acid lipase deficiency - sebelipase alfa [ID737]
In development [GID-LYSOSOMALACIDLIPASEDEFICIENCYSEBELIPASEALFAID737] Expected publication date: TBC
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Afamelanotide for treating erythropoietic protoporphyria [ID927]
In development [GID-HST10009] Expected publication date: TBC
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Avalglucosidase alfa for treating Pompe disease [ID3737]
Proposed [GID-HST10030] Expected publication date: TBC
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Arimoclomol for treating Niemann-Pick disease Type C [ID1312]
Proposed [GID-HST10037] Expected publication date: TBC
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Lonafarnib for treating progeria and progeroid laminopathies [ID3867]
Proposed [GID-HST10039] Expected publication date: TBC
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OTL-200 for treating metachromatic leukodystrophy [ID1666]
In development [GID-HST10028] Expected publication date: 13 August 2021
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Elosulfase alfa for treating mucopolysaccharidosis type IVa (review of HST2) [ID1643]
In development [GID-HST10027] Expected publication date: TBC
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Palovarotene for preventing heterotopic ossification associated with fibrodysplasia ossificans progressiva [ID3739]
In development [GID-HST10032] Expected publication date: TBC
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Palovarotene for treating flare ups of heterotopic ossification associated with fibrodysplasia ossificans progressiva [ID2721]
In development [GID-HST10033] Expected publication date: TBC
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Odevixibat (A 4250) for progressive familial intrahepatic cholestasis [ID1570]
Proposed [GID-HST10043] Expected publication date: TBC
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Lenti-D for treating cerebral adrenoleukodystrophy [ID1284]
Proposed [GID-HST10038] Expected publication date: TBC
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Onasemnogene abeparvovec for treating spinal muscular atrophy type 1 [ID1473]
In development [GID-HST10026] Expected publication date: TBC
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Disabled children and young people up to 25 with severe complex needs: integrated service delivery and organisation across health, social care and education
In development [GID-NG10113] Expected publication date: 19 January 2022
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Advocacy services for adults with health and social care needs
In development [GID-NG10156] Expected publication date: TBC
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Adults with complex needs: social work interventions including assessment, care management and support
In development [GID-NG10145] Expected publication date: 27 April 2022
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Endo-SPONGE for treating low rectal anastomotic leakage (MT461)
In development [GID-MT539] Expected publication date: TBC
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Peezy Midstream for urine collection (MT446)
In development [GID-MT538] Expected publication date: TBC
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The MAGEC system for spinal lengthening in children with scoliosis
In development [GID-MT544] Expected publication date: 15 September 2020
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Leukomed Sorbact for preventing surgical site infection (MTG55)
Evidence-based recommendations on Leukomed Sorbact for preventing surgical site infection after caesarean section or vascular surgery
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DHT pilot: myCOPD for self-management of chronic obstructive pulmonary disease (COPD)
In development [GID-MT531] Expected publication date: TBC
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SecurAcath for securing percutaneous catheters (MTG34)
Evidence-based recommendations on SecurAcath for securing percutaneous catheters (central venous catheters/CVCs)
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Memokath-051 stent for ureteric obstruction (MTG35)
Evidence-based recommendations on Memokath-051 stent for treating ureteric obstruction
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Thopaz+ portable digital system for managing chest drains (MTG37)
Evidence-based recommendations on Thopaz+ for managing chest drains
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Neuropad for detecting preclinical diabetic peripheral neuropathy (MTG38)
Evidence-based recommendations on Neuropad for detecting preclinical diabetic peripheral neuropathy
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iFuse for treating chronic sacroiliac joint pain (MTG39)
Evidence-based recommendations on iFuse for treating chronic sacroiliac joint pain
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HumiGard for preventing inadvertent perioperative hypothermia (MTG31)
Evidence-based recommendations on HumiGard for preventing inadvertent perioperative hypothermia
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HeartFlow FFRCT for estimating fractional flow reserve from coronary CT angiography (MTG32)
Evidence-based recommendations on HeartFlow FFRCT for estimating fractional flow reserve from coronary CT angiography
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ENDURALIFE powered CRT-D devices for treating heart failure (MTG33)
Evidence-based recommendations on ENDURALIFE-powered CRT-D devices for treating heart failure
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Episcissors-60 for mediolateral episiotomy (MTG47)
Evidence-based recommendations on Episcissors-60 for mediolateral episiotomy
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PneuX to prevent ventilator-associated pneumonia (MTG48)
Evidence-based recommendations on PneuX to prevent ventilator-associated pneumonia
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Rezum for treating lower urinary tract symptoms secondary to benign prostatic hyperplasia (MTG49)
Evidence-based recommendations on Rezum for treating lower urinary tract symptoms secondary to benign prostatic hyperplasia
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The MIST Therapy system for the promotion of wound healing (MTG5)
Evidence-based recommendations on the MIST Therapy system for the promotion of wound healing
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Curos for preventing infections when using needleless connectors (MTG44)
Evidence-based recommendations on Curos for preventing infections when using needleless connectors
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Endocuff Vision for assisting visualisation during colonoscopy (MTG45)
Evidence-based decisions on Endocuff Vision for assisting visualisation during colonoscopy
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gammaCore for cluster headache (MTG46)
Evidence-based recommendations on gammaCore for cluster headache
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The geko device for reducing the risk of venous thromboembolism (MTG19)
Evidence-based recommendations on the geko device for reducing the risk of venous thromboembolism
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moorLDI2-BI: a laser doppler blood flow imager for burn wound assessment (MTG2)
Evidence-based recommendations on moorLDI2-BI: a laser doppler blood flow imager for burn wound assessment