- Status:
- Awaiting development
- Technology type:
- Medicine
- Decision:
- Selected
- Reason for decision:
- Anticipate the topic will be of importance to patients, carers, professionals, commissioners and the health of the public to ensure clinical benefit is realised, inequalities in use addressed, and help them make the best use of NHS resources
- Process:
- STA Standard
- ID number:
- 3897
Project Team
- Project lead
- Emily Richards
Email enquiries
If you have any queries please email scopingta@nice.org.uk
Timeline
Key events during the development of the guidance:
| Date | Update |
|---|---|
| 30 June 2025 | Awaiting development. As you will be aware, the Department for Health & Social Care has asked NICE to carry out a Single Technology Appraisal of Delandistrogene moxeparvovec for treating Duchenne muscular dystrophy in children 4 to 7 years. Following on from advice received from the company, timelines for this appraisal are to be confirmed whilst the company confirm their regulatory filing timelines. As this appraisal has been referred NICE will continue to monitor any development and will update interested parties if the situation changes. |
| 18 June 2025 | Awaiting development. As you will be aware, the Department for Health & Social Care has asked NICE to carry out a Single Technology Appraisal of Delandistrogene moxeparvovec for treating Duchenne muscular dystrophy in children 4 to 7 years. Following on from advice received from the company, timelines for this appraisal are to be confirmed whilst the company confirm their regulatory filing timelines. As this appraisal has been referred NICE will continue to monitor any development and will update interested parties if the situation changes. |
| 27 August 2024 | Note - Note added to the project documents |
| 18 January 2024 - 15 February 2024 | Consultation on suggested remit, draft scope and provisional stakeholder list of consultees and commentators: 3897 |
| 18 January 2024 | In progress. Scoping commenced. |
| 24 October 2023 | Awaiting development. Status change linked to Topic Selection Decision being set to Selected |
For further information on our processes and methods, please see our CHTE processes and methods manual