VTS-270 for treating Niemann-Pick type C1 [ID1267]Status:In developmentProgramme:Highly specialised technologies guidanceExpected publication date: TBC
Evinacumab for treating homozygous familial hypercholesterolaemia in people aged 12 years and over [ID2704]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Arimoclomol for treating Niemann-Pick disease Type C [ID1312]Status:In developmentProgramme:Highly specialised technologies guidanceExpected publication date: TBC
Olipudase alfa for treating Niemann-Pick disease types A and B [ID3913 ]Status:In developmentProgramme:Highly specialised technologies guidanceExpected publication date: TBC