Leriglitazone for treating cerebral adrenoleukodystrophy in boys and men 2 years and over [ID3903]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Sodium zirconium cyclosilicate for treating hyperkalaemia (partial review of TA599) [ID6439]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Doxecitine–doxribtimine for treating thymidine kinase 2 deficiency in people of any age [ID6484]Status:In developmentProgramme:Highly specialised technologies guidanceExpected publication date: TBC
Govorestat for treating classic galactosemia in people 2 to 65 years [TSID12071]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC