Polyendocrine Metabolic Ovarian Syndrome (PMOS)Status:In development | In consultationProgramme:NICE guidelineConsultation end date: 11 August 2026Expected publication date: 9 December 2026
Doxecitine–doxribtimine for treating thymidine kinase 2 deficiency in people of any age [ID6484]Status:In developmentProgramme:Highly specialised technologies guidanceExpected publication date: TBC
Govorestat for treating classic galactosemia in people 2 to 65 years [TSID12071]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Rebisufligene etisparvovec for treating mucopolysaccharidosis type IIIA [ID6540]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Elamipretide for treating Barth syndrome in people of any age [ID6545]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC