Information for the public

Strimvelis is available on the NHS as a possible treatment for adenosine deaminase deficiency–severe combined immunodeficiency when there is no suitably matched relative to donate stem cells.

Is this treatment right for my child?

Your child’s healthcare professionals should give you clear information, talk with you about their options and listen carefully to your views and concerns. Read more about making decisions about your care.

Questions to think about

  • How well does it work compared with other treatments?
  • What are the risks or side effects? How likely are they?
  • How will the treatment affect my child’s day-to-day life?
  • What happens if the treatment does not work?
  • What happens if I do not want my child to have treatment? Are there other treatments available?

Information and support

These organisations can give you advice and support:

You can also get support from your local Healthwatch.

NICE is not responsible for the quality or accuracy of any information or advice provided by these organisations.

ISBN: 978-1-4731-2819-4

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