| Companies sponsors |
ITF Pharma UK (givinostat) |
| Others |
Alder Hey Children’s Hospital NHS Foundation Trust, Liverpool |
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Bristol Royal Hospital for Children, Bristol |
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Department of Health and Social Care |
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Dubowitz Neuromuscular Centre (DNC) |
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MD UK Oxford Neuromuscular Centre, Oxford |
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MRC Centre for Neuromuscular Diseases |
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NHS England |
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Queen Square Centre for Neuromuscular Diseases UCL |
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Robert Jones and Agnes Hunt Orthopaedic Hospital, Oswestry |
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Royal Manchester Children’s Hospital NHS Foundation Trust, Manchester |
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Ryegate Centre, Sheffield Children’s NHS Foundation Trust, Sheffield |
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The Addenbrooke’s Neuromuscular Service, Cambridge |
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The John Walton Muscular Dystrophy Research Centre, Newcastle |
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The National Hospital for Neurology and Neurosurgery, London |
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The Walton Centre, Liverpool |
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Wessex Neurological Centre, Southampton General Hospital, Southampton |
| Patient carer groups |
Action Duchenne |
| |
Alex's Wish |
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Arthritis & Musculoskeletal Alliance |
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Beacon |
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Duchenne Family Support Group |
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Duchenne Now |
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Duchenne Research Fund |
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Duchenne UK |
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Gene People |
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Genetic Alliance UK |
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Harrison’s Fund |
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Joining Jack |
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Muscular Dystrophy UK |
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Pathfinders Neuromuscular Alliance |
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South Asian Health Foundation |
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Specialised Healthcare Alliance |
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Together for Short Lives |
| Professional groups |
Association of Anaesthetists of Great Britain & Ireland |
| |
Association of British Neurologists |
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Association of Chartered Physiotherapists in Respiratory Care |
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Association of Genetic Nurses & Counsellors |
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Association of Respiratory Nurse Specialists |
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Association of Surgeons of Great Britain and Ireland |
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British Cardiovascular Society |
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British Dietetic Association |
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British Geriatrics Society |
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British Institute of Musculoskeletal Medicine |
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British Myology Society |
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British Orthopaedic Association |
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British Paediatric and Adolescent Bone Group |
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British Paediatric Neurology Association |
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British Paediatric Respiratory Society |
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British Society for Children's Orthopaedic Surgery |
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British Society for Gene and Cell Therapy |
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British Society for Genetic Medicine |
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British Society for Paediatric Endocrinology and Diabetes |
| |
British Society of Physical and Rehabilitation
|
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British Thoracic Society |
| |
Chartered Society of Physiotherapy |
| |
Neonatal and Paediatric Pharmacists Group |
| |
Primary Care Respiratory Society UK |
| |
Royal College of General Practitioners |
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Royal College of Nursing |
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Royal College of Paediatrics and Child Health |
| |
Royal College of Pathologists |
| |
Royal College of Physicians |
| |
Royal College of Surgeons |
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Royal Pharmaceutical Society |
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Royal Society of Medicine |
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Society for Endocrinology |
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The National Congenital Anomaly and Rare Disease Registration Service |
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The North Star Clinical Network |
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UK Clinical Pharmacy Association |
| Associated public health groups |
Public Health Wales |
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UK Health Security Agency |
| Comparator companies |
PTC Therapeutics (ataluren) |
| General commentators |
All Wales Inherited Metabolic Disease Service |
| |
All Wales Therapeutics and Toxicology Centre |
| |
Allied Health Professionals Federation |
| |
Board of Community Health Councils in Wales |
| |
British National Formulary |
| |
Care Quality Commission |
| |
Cell and Gene Therapy Catapult |
| |
Department of Health - Northern Ireland |
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Healthcare Improvement Scotland |
| |
Medicines and Healthcare products Regulatory Agency |
| |
National Association of Primary Care |
| |
National Pharmacy Association |
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National Services Division |
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NHS Alliance |
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NHS Confederation |
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Scottish Medicines Consortium |
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Welsh Government |
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Welsh Health Specialised Services Committee |
| Relevant research groups |
Bone Research Society |
| |
Cochrane Cystic Fibrosis and Genetic Disorders Group |
| |
Cochrane Musculoskeletal Group |
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Cochrane UK |
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Genomics England |
| |
MRC Centre for Neuromuscular Diseases |
| |
MRC Clinical Trials Unit |
| |
National Institute for Health Research |
| |
Orthopaedic Research UK |
| |
TREAT-NMD |