Status Awaiting development
Technology type Medicine
Decision Selected
Reason for decision Anticipate the topic will be of importance to patients, carers, professionals, commissioners and the health of the public to ensure clinical benefit is realised, inequalities in use addressed, and help them make the best use of NHS resources
Process STA Standard
ID number 3897

Project Team

Project lead Emily Richards

Email enquiries

Timeline

Key events during the development of the guidance:

Date Update
18 June 2025 Awaiting development. As you will be aware, the Department for Health & Social Care has asked NICE to carry out a Single Technology Appraisal of Delandistrogene moxeparvovec for treating Duchenne muscular dystrophy in children 4 to 7 years. Following on from advice received from the company, timelines for this appraisal are to be confirmed whilst the company confirm their regulatory filing timelines. As this appraisal has been referred NICE will continue to monitor any development and will update interested parties if the situation changes.
27 August 2024 Please note that following on from advice received from the company this appraisal has been rescheduled to align with latest regulatory expectations. Therefore, we now anticipate that the appraisal will begin during early October 2025 when we will write to you about how you can get involved. The deadline for submissions is expected in approximately early December 2025.
18 January 2024 - 15 February 2024 Consultation on suggested remit, draft scope and provisional stakeholder list of consultees and commentators: 3897
18 January 2024 In progress. Scoping commenced.
24 October 2023 Awaiting development. Status change linked to Topic Selection Decision being set to Selected

For further information on our processes and methods, please see our CHTE processes and methods manual