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2 Information about elosulfase alfa

Marketing authorisation indication

2.1 Elosulfase alfa (Vimizim, Biomarin) is licensed to treat 'mucopolysaccharidosis, type IVA (Morquio A Syndrome, MPS IVA) in patients of all ages'.


2.3 The price for elosulfase alfa is £750 per 5 mg vial (excluding VAT; BNF online accessed October 2021). The company has a commercial arrangement, which would have applied if the technology had been recommended.