1. Home
  2. NICE Guidance
  3. Conditions and diseases
  4. Musculoskeletal conditions
  5. Spinal conditions

Risdiplam for treating spinal muscular atrophy

Technology appraisal guidance [TA755] Published: 16 December 2021

  • Guidance
  • Tools and resources
  • Information for the public
  • Evidence
  • History

Evidence

Review and download supporting evidence. Includes the full guideline if available.

Supporting evidence

  • Evaluation report  
  • Appraisal consultation committee papers PDF 5.48 MB 16 December 2021  
  • Final appraisal determination committee papers PDF 2.56 MB 16 December 2021