History A list of downloadable documents created during development. Expected publication Equality Impact Assessment (Guidance development) PDF 166 KB 16 December 2021 Register of interests PDF 164 KB 16 December 2021 Final draft guidance Final draft guidance Final appraisal document PDF 331 KB 19 November 2021 Committee papers PDF 2.56 MB 19 November 2021 Public committee slides PDF 1.45 MB 19 November 2021 Final appraisal document Managed Access Agreement PDF 270 KB 19 November 2021 Final appraisal document Data Collection Arrangement PDF 246 KB 19 November 2021 Final appraisal document Appendix A - Using other treatments after onasemnogene PDF 129 KB 19 November 2021 Final appraisal document Appendix B - Managed Access Patient Agreement form PDF 110 KB 19 November 2021 Draft guidance Draft guidance Appraisal consultation document (PDF version) PDF 321 KB 02 June 2021 Appraisal consultation document (online commenting) Committee papers PDF 5.48 MB 02 June 2021 Public committee slides PDF 1.12 MB 02 June 2021 Invitation to participate Final scope PDF 195 KB 27 August 2020 Final stakeholder list PDF 214 KB 27 August 2020 NICE's response to comments on the draft scope and provisional stakeholder list PDF 848 KB 27 August 2020 Equality impact assessment (Scoping) PDF 127 KB 27 August 2020 Consultation on suggested remit, draft scope and provisional stakeholder list of consultees and commentators Consultation on suggested remit, draft scope and provisional stakeholder list of consultees and commentators Draft scope pre referral PDF 215 KB 03 February 2020 Draft matrix pre referral PDF 230 KB 03 February 2020