Awaiting development: Guidance and quality standards
Showing 1 to 2 of 2
| Title | Type |
|---|---|
| OTL-101 for treating adenosine deaminase deficiency–severe combined immunodeficiency [ID1152] | Highly specialised technology |
| Setmelanotide for treating obesity and hyperphagia in Bardet-Biedl syndrome (review of HST31) [ID6598] | Highly specialised technology |