In development: Guidance, quality standards and advice

Skip to filtersSkip to results

Skip to results

Keyword or reference number

Keyword or reference number

Expected publication date

Expected publication date

Type

Type

Guidance programme 1 selected

Guidance programme

Showing 1 to 4 of 4

TitleTypeExpected publication date
Arimoclomol for treating Niemann-Pick disease Type C [ID1312]Highly specialised technologyTBC
Doxecitine–doxribtimine for treating thymidine kinase 2 deficiency in people of any age [ID6484]Highly specialised technologyTBC
Setmelanotide for treating obesity and hyperphagia in Bardet-Biedl syndrome (review of HST31) [ID6598]Highly specialised technology
Tofersen for treating amyotrophic lateral sclerosis caused by SOD1 gene mutations [ID3767]Highly specialised technology

Results per page

  1. 10
  2. 25
  3. 50
  4. All