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Topic prioritisation
Title
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Decision
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Leniolisib for untreated activated phosphoinositide 3-kinase delta syndrome in
children
4 to 11 years [TSID12190]
None selected
Not selected
16 June 2025
Sulthiame for treating self-limiting epilepsy with centrotemporal spikes in
children
TSID 12106
None selected
Not selected
30 April 2025
Ustekinumab for treating moderately to severely active ulcerative colitis in
children
aged 2 to 17 years [TSID 12128]
None selected
Not selected
4 February 2025
Berotralstat for preventing recurrent attacks of hereditary angioedema in
children
aged 2 to 12 years [TSID 12132]
None selected
Not selected
4 February 2025
Lebrikizumab for treating atopic dermatitis in
children
[TSID12133]
None selected
Not selected
4 February 2025
Lebrikizumab for treating atopic dermatitis in
children
[TSID 12133_TSID 12135]
None selected
Not selected
4 February 2025
Pitolisant for treating narcolepsy in
children
and young people 6 to 17 years ID6353
None selected
Not selected
9 December 2024
Selumetinib granules for treating symptomatic and inoperable plexiform neurofibromas associated with type 1 neurofibromatosis in
children
1 to 6 years [TSID12092]
None selected
Not selected
14 November 2024
Evinacumab for treating homozygous familial hypercholesterolemia in
children
aged 6 months to 11 [TSID11806]
None selected
Not selected
1 November 2024
Ustekinumab for the treatment of moderately to severely active Crohn's disease in
children
[TS ID 11955]
None selected
n/a
10 September 2024
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