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Topic prioritisation
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NVK-002 for treating myopia
in
people 3 to 17 years [TSID11961]
None selected
Not selected
12 December 2024
Pitolisant for treating narcolepsy
in
children and young people 6 to 17 years ID6353
None selected
Not selected
9 December 2024
Entrectinib for treating NTRK fusion-positive solid tumours
in
people 1 month to 11 years [TSID12116]
None selected
Not selected
14 November 2024
Selumetinib granules for treating symptomatic and inoperable plexiform neurofibromas associated with type 1 neurofibromatosis
in
children 1 to 6 years [TSID12092]
None selected
Not selected
14 November 2024
Evinacumab for treating homozygous familial hypercholesterolemia
in
children aged 6 months to 11 [TSID11806]
None selected
Not selected
1 November 2024
Lomitapide for treating homozygous familial hypercholesterolaemia
in
people 5 to 17 years [TSID 12085]
None selected
Not selected
24 October 2024
Ustekinumab for the treatment of moderately to severely active Crohn's disease
in
children [TS ID 11955]
None selected
n/a
10 September 2024
Mexiletine hydrochloride for treating myotonia
in
children and adolescents with myotonic disorders [TS ID 11978]
None selected
Not selected
10 September 2024
Human normal immunoglobulin for preventing infection
in
chronic lymphocytic leukaemia [TSID12043]
None selected
Not selected
10 September 2024
Budesonide–glycopyrronium–formoterol fumarate for treating severe asthma
in
people 12 years and over TS ID 12018
None selected
Not selected
12 August 2024
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