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Showing 2476 to 2490 of 8213 results
Awaiting development Reference number: GID-TA11765 Expected publication date: TBC
Tofersen for treating amyotrophic lateral sclerosis caused by SOD1 gene mutations [ID3767]
In development Reference number: GID-HST10062 Expected publication date: TBC
In development Reference number: GID-MT526 Expected publication date: TBC
Givinostat for treating Duchenne muscular dystrophy in people 6 years and over [ID6323]
In development Reference number: GID-TA11373 Expected publication date: TBC
In development Reference number: GID-TA11590 Expected publication date: TBC
In development Reference number: GID-TA11862 Expected publication date: TBC
In development Reference number: GID-TA11813 Expected publication date: TBC
In development Reference number: GID-TA11801 Expected publication date: TBC
In development Reference number: GID-TA11330 Expected publication date: TBC
In development Reference number: GID-TA11439 Expected publication date: TBC
Maralixibat for treating cholestatic pruritus in Alagille syndrome [ID3941]
In development Reference number: GID-TA10832 Expected publication date: TBC
In development Reference number: GID-NG10398 Expected publication date: 19 March 2026
Metabolic Dysfunction-Associated Steatotic Liver Disease (MASLD)
In development Reference number: GID-NG10434 Expected publication date: 02 December 2026
In development Reference number: GID-TA11804 Expected publication date: 08 October 2026
Awaiting development Reference number: GID-TA11828 Expected publication date: TBC