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Discontinued Reference number: GID-MT81
Discontinued Reference number: GID-PHG0
Maternal health: promoting maternal health through community based strategies
Discontinued Reference number: GID-QS10016
Discontinued Reference number: GID-DT9
Drisapersen for the first-line treatment of Duchenne's muscular dystrophy [ID911]
Discontinued Reference number: GID-HST10004
Eteplirsen for treating Duchenne muscular dystrophy [ID1003]
Discontinued Reference number: GID-HST10007
Intrathecal idursulfase for treating Mucopolysaccharidosis type II ID1223
Discontinued Reference number: GID-HST10019
In development Reference number: GID-HST10020 Expected publication date: TBC
Arimoclomol for treating Niemann-Pick disease Type C [ID1312]
In development Reference number: GID-HST10037 Expected publication date: TBC
Elivaldogene autotemcel for treating cerebral adrenoleukodystrophy [ID1284]
Discontinued Reference number: GID-HST10038
Discontinued Reference number: GID-QS10108
Discontinued Reference number: GID-SGWAVE0701
Discontinued Reference number: GID-SGWAVE0702
Discontinued Reference number: GID-SGWAVE0761
Discontinued Reference number: GID-SGWAVE0762