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Discontinued Reference number: GID-HST10033
In development Reference number: GID-TA11449 Expected publication date: TBC
Discontinued Reference number: GID-NG10377
Discontinued Reference number: GID-TA10891
Discontinued Reference number: GID-TA10297
Discontinued Reference number: GID-TA10390
Ataluren for treating cystic fibrosis in people with a CFTR gene nonsense mutation [ID955]
Discontinued Reference number: GID-TA11262
Discontinued Reference number: GID-TA10110
Discontinued Reference number: GID-TA11260
In development Reference number: GID-TA11670 Expected publication date: TBC
In development Reference number: GID-TA11760 Expected publication date: TBC
Resminostat for maintenance treatment of advanced mycosis fungoides or Sezary syndrome [ID6478]
In development Reference number: GID-TA11606 Expected publication date: TBC
OTL-101 for treating adenosine deaminase deficiency–severe combined immunodeficiency [ID1152]
Discontinued Reference number: GID-HST10022
Giroctocogene fitelparvovec for treating moderately severe to severe haemophilia A [ID6312]
Discontinued Reference number: GID-TA11329
In development Reference number: GID-TA11808 Expected publication date: TBC