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Discontinued Reference number: GID-TA11401
Discontinued Reference number: GID-TA11093
Discontinued Reference number: GID-TA11433
Discontinued Reference number: GID-TA11163
Discontinued Reference number: GID-TA10568
Discontinued Reference number: GID-TA11089
Repotrectinib for treating ROS1-positive advanced non-small-cell lung cancer [ID6277]
Discontinued Reference number: GID-TA11302
Discontinued Reference number: GID-TA11007
Intrathecal idursulfase for treating Mucopolysaccharidosis type II ID1223
Discontinued Reference number: GID-HST10019
Elivaldogene autotemcel for treating cerebral adrenoleukodystrophy [ID1284]
Discontinued Reference number: GID-HST10038
Eteplirsen for treating Duchenne muscular dystrophy [ID1003]
Discontinued Reference number: GID-HST10007
Drisapersen for the first-line treatment of Duchenne's muscular dystrophy [ID911]
Discontinued Reference number: GID-HST10004
Arimoclomol for treating Niemann-Pick disease Type C [ID1312]
In development Reference number: GID-HST10037 Expected publication date: TBC
Discontinued Reference number: GID-MT117
Discontinued Reference number: GID-MT163