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Guidance (178)
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Highly specialised technologies guidance (2)
Technology appraisal guidance (176)
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Showing 51 to 100 of 178
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Guidance and quality standards awaiting development
Title
Type
Elamipretide for
treating
Barth syndrome in people of any age [ID6545]
Technology appraisal guidance
Elinzanetant for
treating
vasomotor symptoms associated with menopause [ID6359]
Technology appraisal guidance
Elinzanetant for
treating
vasomotor symptoms caused by adjuvant endocrine treatment to prevent or treat hormone-receptor positive breast cancer [ID6544]
Technology appraisal guidance
Elranatamab for
treating
relapsed or refractory multiple myeloma after 2 treatments [ID6464]
Technology appraisal guidance
Elranatamab for
treating
relapsed or refractory multiple myeloma after treatments including anti-CD38 antibody and lenalidomide therapy [ID6591]
Technology appraisal guidance
Eneboparatide for
treating
chronic hypoparathyroidism [TSID12145]
Technology appraisal guidance
Enlicitide decanoate for
treating
hyperlipidaemia in people at risk of an atherosclerotic cardiovascular disease event [ID6656]
Technology appraisal guidance
Eplontersen for
treating
transthyretin-related amyloidosis cardiomyopathy [TSID12015]
Technology appraisal guidance
Estetrol for
treating
vasomotor symptoms associated with the menopause in people aged 40 to 65 [ID4037]
Technology appraisal guidance
Etrolizumab for
treating
moderately to severely active ulcerative colitis [ID3827]
Technology appraisal guidance
Fenebrutinib for
treating
primary progressive multiple sclerosis [ID6543]
Technology appraisal guidance
Fenebrutinib for
treating
relapsing multiple sclerosis [ID6577]
Technology appraisal guidance
Fostemsavir for
treating
adults with multidrug resistant HIV-1 for whom it is not possible to construct a suppressive anti-viral regimen [ID2726]
Technology appraisal guidance
Gantenerumab for
treating
early Alzheimer's disease [TSID10668]
Technology appraisal guidance
Gemcitabine intravesical delivery system for
treating
high-risk non-muscle-invasive bladder cancer untreated with BCG [ID6658]
Technology appraisal guidance
Gemcitabine intravesical delivery system for
treating
recurrent high-risk papillary non-muscle-invasive bladder after BCG [ID6657]
Technology appraisal guidance
Gosuranemab for
treating
progressive supranuclear palsy [ID1607]
Technology appraisal guidance
Ibalizumab for
treating
adults infected with multidrug resistant HIV-1 for whom it is not possible to construct a suppressive anti-viral regimen [ID2720]
Technology appraisal guidance
Imetelstat for
treating
intermediate-2 or high-risk relapsed or refractory myelofibrosis after a JAK inhibitor [TSID8376]
Technology appraisal guidance
Inclisiran for
treating
familial hypercholesterolaemia and elevated low density lipoprotein cholesterol in people 12 to 17 years [TSID12129]
Technology appraisal guidance
Inebilizumab for
treating
AQP4-IgG-seropositive neuromyelitis optica spectrum disorders [ID6430]
Technology appraisal guidance
Inebilizumab for
treating
generalised myasthenia gravis [ID6587] [TSID12110]
Technology appraisal guidance
Inebilizumab for
treating
immunoglobulin G4-related disease [TSID12107]
Technology appraisal guidance
Invimestrocel for
treating
acute ischaemic stroke within 18 to 36 hours of onset [TSID10190]
Technology appraisal guidance
Invoseltamab for
treating
relapsed or refractory multiple myeloma after 3 or more treatments [ID6609]
Technology appraisal guidance
Iptacopan for
treating
primary IgA nephropathy [ID6640]
Technology appraisal guidance
Irbesartan–propagermanium for
treating
focal segmental glomerulosclerosis in people 12 years and over having an angiotensin II receptor blocker [ID6469]
Technology appraisal guidance
Istradefylline with levodopa for
treating
motor fluctuations in Parkinson's disease [ID3868]
Technology appraisal guidance
Ixekizumab for
treating
enthesitis-related arthritis and juvenile psoriatic arthritis in people 2 to 17 years [ID6590]
Technology appraisal guidance
LAM-561 with radiotherapy and temozolomide for
treating
IDH1 wild-type glioblastoma [ID4022]
Technology appraisal guidance
Larotrectinib for
treating
NTRK fusion-positive advanced solid tumours (MA review of TA630) [ID6292]
Technology appraisal guidance
Leriglitazone for
treating
X-linked andrenoleukodystrophy [TSID9996]
Technology appraisal guidance
Letetresgene autoleucel for
treating
NY-ESO-1 advanced unresectable synovial sarcoma in people aged 10 and over or NY-ESO-1 advanced unresectable myxoid round cell liposarcoma in adults [TSID10652]
Technology appraisal guidance
Liposomal cytarabine–daunorubicin for
treating
relapsed or refractory acute myeloid leukaemia in people aged 1 to 21 years [ID4017]
Technology appraisal guidance
Lisocabtagene maraleucel for
treating
relapsed or refractory low-grade B-cell follicular lymphoma after 1 or more treatments [ID6564]
Technology appraisal guidance
Luspatercept for
treating
anaemia in non-transfusion dependent beta-thalassaemia [ID3870]
Technology appraisal guidance
Marstacimab for
treating
severe haemophilia A or B in people 12 years and over with inhibitors to factor-replacement therapy [TSID12143]
Technology appraisal guidance
Mavorixafor for
treating
WHIM syndrome [ID3946]
Technology appraisal guidance
Mevrometostat with enzalutamide for
treating
hormone-relapsed metastatic prostate cancer after abiraterone acetate [TSID12239]
Technology appraisal guidance
Mosunetuzumab with lenalidomide for
treating
relapsed or refractory follicular lymphoma after 1 or more systemic treatments [ID6655]
Technology appraisal guidance
Naxitamab with GM-CSF for
treating
relapsed or refractory high-risk neuroblastoma [ID3769]
Technology appraisal guidance
Nedosiran
treating
primary hyperoxaluria type 1 in people 6 years and over [TSID11777]
Technology appraisal guidance
Netarsudil for
treating
open angle glaucoma or ocular hypertension [ID1078]
Technology appraisal guidance
Niraparib with abiraterone acetate and prednisone for
treating
hormone-sensitive metastatic prostate cancer [ID6595]
Technology appraisal guidance
Norucholic acid for
treating
primary sclerosing cholangitis [ID6583]
Technology appraisal guidance
Obinutuzumab for
treating
serologically active extra-renal lupus [TSID12285]
Technology appraisal guidance
Odevixibat for
treating
biliary atresia in children following Kasai hepatoportoenterostomy [ID6627]
Technology appraisal guidance
Odronextamab for
treating
relapsed or refractory follicular lymphoma [TSID12236]
Technology appraisal guidance
Omecamtiv mecarbil for
treating
chronic heart failure with reduced ejection fraction [ID3912]
Technology appraisal guidance
Ondansetron for
treating
alcohol-use disorder [ID6341]
Technology appraisal guidance
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