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Showing 2626 to 2640 of 8912 results
Rebisufligene etisparvovec for treating mucopolysaccharidosis type IIIA [ID6540]
Awaiting development Reference number: GID-TA11701 Expected publication date: TBC
Awaiting development Reference number: GID-TA11437 Expected publication date: TBC
AK-OTOF for treating hearing loss caused by otoferlin gene variants [ID6735]
Awaiting development Reference number: GID-TA11962 Expected publication date: TBC
Awaiting development Reference number: GID-TA11940 Expected publication date: TBC
Awaiting development Reference number: GID-TA11760 Expected publication date: TBC
Awaiting development Reference number: GID-TA11499 Expected publication date: TBC
Triheptanoin for treating long-chain fatty acid oxidation disorders [ID3891]
Awaiting development Reference number: GID-TA11473 Expected publication date: TBC
In development Reference number: GID-TA11963 Expected publication date: TBC
In development Reference number: GID-HST10067 Expected publication date: 19 August 2026
Awaiting development Reference number: GID-TA11657 Expected publication date: 07 April 2027
Awaiting development Reference number: GID-TA11584 Expected publication date: 08 December 2027
Awaiting development Reference number: GID-TA11085 Expected publication date: TBC
Vimseltinib for treating tenosynovial giant cell tumours when surgery is unsuitable [ID6736]
Awaiting development Reference number: GID-TA11964 Expected publication date: TBC
Awaiting development Reference number: GID-TA11336 Expected publication date: TBC