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Awaiting development Reference number: GID-TA11658 Expected publication date: TBC
Awaiting development Reference number: GID-TA11224 Expected publication date: TBC
Awaiting development Reference number: GID-TA11425 Expected publication date: TBC
Awaiting development Reference number: GID-TA11229 Expected publication date: TBC
In development Reference number: GID-QS10200 Expected publication date: 16 February 2027
Awaiting development Reference number: GID-TA11497 Expected publication date: TBC
In development Reference number: GID-QS10202 Expected publication date: 06 May 2026
Awaiting development Reference number: GID-TA11583 Expected publication date: TBC
Awaiting development Reference number: GID-TA11308 Expected publication date: TBC
Awaiting development Reference number: GID-TA11162 Expected publication date: 28 July 2027
Rebisufligene etisparvovec for treating mucopolysaccharidosis type IIIA [ID6540]
Awaiting development Reference number: GID-TA11701 Expected publication date: TBC
Awaiting development Reference number: GID-TA11437 Expected publication date: TBC
AK-OTOF for treating hearing loss caused by otoferlin gene variants [ID6735]
Awaiting development Reference number: GID-TA11962 Expected publication date: TBC
Awaiting development Reference number: GID-TA11940 Expected publication date: TBC